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Peer-reviewedCC BY-NC-NDMolecular Therapy Advances

Rapamycin nanoparticles mitigate anti-AAV antibody formation in a mouse model of ornithine transcarbamylase deficiency

  • Antonio Vicidomini
  • Florence Boisgerault
  • Giulia Romano
  • Corrado Guarnaccia
  • Pauline Vidal
  • Fanny Collaud
  • Leandro Soria
  • Giulia de Sabbata
  • Novella Tedesco
  • Michela Lisjak
  • Himanshi Saxena
  • Luca Camparini
9 more authors
  • Alessandra Iaconcig
  • Laura Moretti
  • Natasa Skoko
  • Petr Ilyinskii
  • Nicola Brunetti-Pierri
  • Giulia Bortolussi
  • Giuseppe Ronzitti
  • Takashi Kei Kishimoto
  • Andrés Muro
Open at sourceDOICite

Abstract

mice and may enable AAV vector re-administration, although further optimization is required for clinical translation.

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Cite

BibTeXRIS
BibTeX
@article{vicidomini2026rapamycin,
  title = {{Rapamycin nanoparticles mitigate anti-AAV antibody formation in a mouse model of ornithine transcarbamylase deficiency}},
  author = {Antonio Vicidomini and Florence Boisgerault and Giulia Romano and Corrado Guarnaccia and Pauline Vidal and Fanny Collaud and Leandro Soria and Giulia de Sabbata and Novella Tedesco and Michela Lisjak and Himanshi Saxena and Luca Camparini and Alessandra Iaconcig and Laura Moretti and Natasa Skoko and Petr Ilyinskii and Nicola Brunetti-Pierri and Giulia Bortolussi and Giuseppe Ronzitti and Takashi Kei Kishimoto and Andrés Muro},
  journal = {Molecular Therapy Advances},
  year = {2026},
  month = sep,
  doi = {10.1016/j.omta.2026.201793},
  url = {https://hal.science/hal-05769467v1},
  note = {CC BY-NC-ND},
}
RIS
TY  - JOUR
TI  - Rapamycin nanoparticles mitigate anti-AAV antibody formation in a mouse model of ornithine transcarbamylase deficiency
AU  - Antonio Vicidomini
AU  - Florence Boisgerault
AU  - Giulia Romano
AU  - Corrado Guarnaccia
AU  - Pauline Vidal
AU  - Fanny Collaud
AU  - Leandro Soria
AU  - Giulia de Sabbata
AU  - Novella Tedesco
AU  - Michela Lisjak
AU  - Himanshi Saxena
AU  - Luca Camparini
AU  - Alessandra Iaconcig
AU  - Laura Moretti
AU  - Natasa Skoko
AU  - Petr Ilyinskii
AU  - Nicola Brunetti-Pierri
AU  - Giulia Bortolussi
AU  - Giuseppe Ronzitti
AU  - Takashi Kei Kishimoto
AU  - Andrés Muro
PY  - 2026
DA  - 2026/09/29
JO  - Molecular Therapy Advances
DO  - 10.1016/j.omta.2026.201793
UR  - https://hal.science/hal-05769467v1
AB  - mice and may enable AAV vector re-administration, although further optimization is required for clinical translation.
SN  - 3117-387X
SN  - 3117-387X
ER  -