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PreprintAll rights reservedbioRxiv

KLHL40 gene replacement therapy in severe nemaline myopathy improves survival and skeletal muscle function in a preclinical mouse model

  • G. R. Tate
  • J. McNulty
  • J. Widrick
  • V. A. Gupta1
  1. 1Brigham and Women's Hospital
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Cite

BibTeXRIS
BibTeX
@misc{tate2026klhl40,
  title = {{KLHL40 gene replacement therapy in severe nemaline myopathy improves survival and skeletal muscle function in a preclinical mouse model}},
  author = {G. R. Tate and J. McNulty and J. Widrick and V. A. Gupta},
  howpublished = {bioRxiv},
  year = {2026},
  month = sep,
  doi = {10.64898/2026.09.23.753846},
  url = {https://www.biorxiv.org/content/10.64898/2026.09.23.753846v1},
}
RIS
TY  - UNPB
TI  - KLHL40 gene replacement therapy in severe nemaline myopathy improves survival and skeletal muscle function in a preclinical mouse model
AU  - G. R. Tate
AU  - J. McNulty
AU  - J. Widrick
AU  - V. A. Gupta
PY  - 2026
DA  - 2026/09/23
PB  - bioRxiv
DO  - 10.64898/2026.09.23.753846
UR  - https://www.biorxiv.org/content/10.64898/2026.09.23.753846v1
ER  -