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Functional validation of allele-specific LMNB1 silencing in patient-derived astrocytes as a therapeutic option for Autosomal Dominant Leukodystrophy

  • M. Lorenzati1
  • A. Contato
  • F. Josa-Prado
  • M. Ribodino
  • M. K. Ardakani
  • E. Nicorvo
  • E. Signorino
  • G. Turrini
  • V. Cerrato
  • R. Parolisi
  • F. Lucchini
  • G. Piacenti
11 more authors
  • G. Donati
  • V. Proserpio
  • J. A. Garcia-Leon
  • M. Rossato
  • L. Conti
  • A. Brusco
  • G. Ramazzotti
  • S. Ratti
  • P. Cortelli
  • E. Giorgio
  • A. Buffo
  1. 1University of Turin, Neuroscience Institute Cavalieri Ottolenghi
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BibTeXRIS
BibTeX
@misc{lorenzati2026functional,
  title = {{Functional validation of allele-specific LMNB1 silencing in patient-derived astrocytes as a therapeutic option for Autosomal Dominant Leukodystrophy}},
  author = {M. Lorenzati and A. Contato and F. Josa-Prado and M. Ribodino and M. K. Ardakani and E. Nicorvo and E. Signorino and G. Turrini and V. Cerrato and R. Parolisi and F. Lucchini and G. Piacenti and G. Donati and V. Proserpio and J. A. Garcia-Leon and M. Rossato and L. Conti and A. Brusco and G. Ramazzotti and S. Ratti and P. Cortelli and E. Giorgio and A. Buffo},
  howpublished = {bioRxiv},
  year = {2026},
  month = sep,
  doi = {10.64898/2026.09.09.747273},
  url = {https://www.biorxiv.org/content/10.64898/2026.09.09.747273v1},
}
RIS
TY  - UNPB
TI  - Functional validation of allele-specific LMNB1 silencing in patient-derived astrocytes as a therapeutic option for Autosomal Dominant Leukodystrophy
AU  - M. Lorenzati
AU  - A. Contato
AU  - F. Josa-Prado
AU  - M. Ribodino
AU  - M. K. Ardakani
AU  - E. Nicorvo
AU  - E. Signorino
AU  - G. Turrini
AU  - V. Cerrato
AU  - R. Parolisi
AU  - F. Lucchini
AU  - G. Piacenti
AU  - G. Donati
AU  - V. Proserpio
AU  - J. A. Garcia-Leon
AU  - M. Rossato
AU  - L. Conti
AU  - A. Brusco
AU  - G. Ramazzotti
AU  - S. Ratti
AU  - P. Cortelli
AU  - E. Giorgio
AU  - A. Buffo
PY  - 2026
DA  - 2026/09/09
PB  - bioRxiv
DO  - 10.64898/2026.09.09.747273
UR  - https://www.biorxiv.org/content/10.64898/2026.09.09.747273v1
ER  -