Peer-reviewedCC BYGenes
PHD Inhibitor Vadadustat: The First Drug Therapy for Triosephosphate Isomerase Deficiency
7 affiliations
- 1Pediatric Neurology Unit, Department of Pediatrics, Centre Hospitalier de Luxembourg, L-1210 Luxembourg, Luxembourg
- 2Department of Pharmacology & Chemical Biology, University of Pittsburgh School of Medicine, Pittsburgh, PA 15260, USA; (P.P.); (S.S.); (P.R.); (J.R.F.); (E.R.D.); (C.C.); (M.C.); (K.M.); (G.C.); (G.E.H.)
- 3Clinical Biology Unit, Department of Biochemistry, Centre Hospitalier de Luxembourg, L-1210 Luxembourg, Luxembourg
- 4National Center of Genetics, Laboratoire National de Santé, L-3555 Dudelange, Luxembourg
- 5Department of Pharmacology and Toxicology, University of Arizona College of Pharmacy, Tucson, AZ 85721, USA; (N.K.); (J.J.G.)
- 6Department of Computational & Systems Biology, Organ Pathobiology and Therapeutics Institute, University of Pittsburgh School of Medicine, Pittsburgh, PA 15260, USA; (L.L.V.); (A.V.)
- 7Department of Haematology, Center for Benign Haematology, Thrombosis and Haemostasis, University Medical Centre, 3511 ZK Utrecht, The Netherlands
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BibTeX
@article{scalais2026inhibitor,
title = {{PHD Inhibitor Vadadustat: The First Drug Therapy for Triosephosphate Isomerase Deficiency}},
author = {Emmanuel Scalais and Priyal Patel and Sidney Satterfield and Mylène Donge and Raphael Laschiazza and Arthur Sorlin and Presley Roberts and Joseph R. Figura and Ella R. Donahue and Cindy Cui and Maci Chambers and Kaitlin McClure and Grace Coleman and Naoya Kitamura and James J. Galligan and Laura L. Vollmer and Gregg E. Homanics and Eduard J. van Beers and Andreas Vogt and Michael J. Palladino},
journal = {Genes},
year = {2026},
month = sep,
url = {https://europepmc.org/article/PMC/PMC13704587},
note = {CC BY},
}
RIS
TY - JOUR
TI - PHD Inhibitor Vadadustat: The First Drug Therapy for Triosephosphate Isomerase Deficiency
AU - Emmanuel Scalais
AU - Priyal Patel
AU - Sidney Satterfield
AU - Mylène Donge
AU - Raphael Laschiazza
AU - Arthur Sorlin
AU - Presley Roberts
AU - Joseph R. Figura
AU - Ella R. Donahue
AU - Cindy Cui
AU - Maci Chambers
AU - Kaitlin McClure
AU - Grace Coleman
AU - Naoya Kitamura
AU - James J. Galligan
AU - Laura L. Vollmer
AU - Gregg E. Homanics
AU - Eduard J. van Beers
AU - Andreas Vogt
AU - Michael J. Palladino
PY - 2026
DA - 2026/09/26
JO - Genes
UR - https://europepmc.org/article/PMC/PMC13704587
SN - 2073-4425
ER -