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PreprintAll rights reservedbioRxiv

Structural engineering of dual-targeting antisense oligonucleotides enhances exon 44 skipping for treating Duchenne muscular dystrophy

  • G. Shoffner
  • F. Barthelemy
  • J. Pi
  • S. Manoian
  • B. T. Nguyen
  • I. Little
  • S. F. Nelson
  • M. C. Miceli
  • F. Guo1
  1. 1University of California, Los Angeles
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Cite

BibTeXRIS
BibTeX
@misc{shoffner2026structural,
  title = {{Structural engineering of dual-targeting antisense oligonucleotides enhances exon 44 skipping for treating Duchenne muscular dystrophy}},
  author = {G. Shoffner and F. Barthelemy and J. Pi and S. Manoian and B. T. Nguyen and I. Little and S. F. Nelson and M. C. Miceli and F. Guo},
  howpublished = {bioRxiv},
  year = {2026},
  month = oct,
  doi = {10.64898/2026.10.01.754576},
  url = {https://www.biorxiv.org/content/10.64898/2026.10.01.754576v1},
}
RIS
TY  - UNPB
TI  - Structural engineering of dual-targeting antisense oligonucleotides enhances exon 44 skipping for treating Duchenne muscular dystrophy
AU  - G. Shoffner
AU  - F. Barthelemy
AU  - J. Pi
AU  - S. Manoian
AU  - B. T. Nguyen
AU  - I. Little
AU  - S. F. Nelson
AU  - M. C. Miceli
AU  - F. Guo
PY  - 2026
DA  - 2026/10/01
PB  - bioRxiv
DO  - 10.64898/2026.10.01.754576
UR  - https://www.biorxiv.org/content/10.64898/2026.10.01.754576v1
ER  -